Loading...

APBDRF Next Steps: Patient Registry

323 views

Loading...

Loading...

Transcript

The interactive transcript could not be loaded.

Loading...

Loading...

Rating is available when the video has been rented.
This feature is not available right now. Please try again later.
Published on Aug 10, 2012

Since treatments for genetic diseases have been found there has been a major shift in acceptance of patient registries. APBD patients can be assured the registry would be maintained in an anonymous and protected way, ensuring confidentiality. Registries provide a natural history of a disease. If you can show you can alter the natural history of a genetic disorder favorably and improve quality of life by comparing it with the untreated state from a registry, then you're much better positioned to get FDA approval for new treatments and new drugs.




Directed by Tom Basis
www.apbdrf.org

Loading...

When autoplay is enabled, a suggested video will automatically play next.

Up next


to add this to Watch Later

Add to

Loading playlists...