First targeted treatment success for Duchenne muscular dystrophy
Loading...
Uploaded by GlobalHealthChannel on Jul 25, 2011
Scientists at the UCL Institute of Child Health (ICH) have led on an important breakthrough in the development of a treatment for Duchenne muscular dystrophy, as detailed in The Lancet today.
Together with the MDEX Consortium where the ICH's Prof Francesco Muntoni is the Chair, the group have shown that an antisense oligonucleotide genetic therapy was effective in restoring the missing protein dystrophin in 7/19 trial participants, with 3 in the higher dose cohort showing for the first time levels in dystrophin exceeding 18% of those found in normal muscle. Their laboratory findings suggest that this approach could provide a functional advantage to affected patients with eligible mutations.
- 7 likes, 0 dislikes
-
- 2:51
Duchenne Teen Receives STS Treatmentby MistyVanderWeele2,531 views
- 0:23
Duchenne's Signby PalmerNMS2,846 views
- 6:13
Testimonial for Fetal Stem Cell Treatment of Duchenne Muscular Dystrophyby emcellsite594 views
- 0:09
Duchenne's Muscular Dystrophy Stem Cell Treatment - Reelabs Indiaby reelabs3,349 views
- 4:28
Stem Cell Therapy For Duchenne Muscular Dystrophy, Mumbaiby neurogenbsi784 views
- 3:51
Dance your PhD 2011by kemaladewi24,231 views
- 5:43
Duchenne Timeline.wmvby rainrtr50,700 views
- 4:34
CureDuchenne 2011 - Cure Duchenne - Experts on Duchenne Muscular Dystrophyby CureDuchenneMD3,295 views
- 4:01
Duchenne, Is Steriods Best Treatment?by duchennemom459 views
- 5:15
Chinese Lanterns in aid of Duchenne Muscular Dystrophy - Ilfracombe 2011 in 3Dby croccy22237 views
- 0:57
A Message From Coalition Duchenneby CoalitionDuchenne261 views
- 5:11
Dalton Defeating Duchenne ~ Blessingsby stacieal2,424 views
- 4:10
Antisense Therapy and the creation of the SOD1 protein.by TheHandofAnimation2,068 views
- 0:45
Curing Muscular Dystrophyby stemcellfoundation1,255 views
- 2:58
Muscular dystrophyby OUlearn813 views
- 1:26
Robust Quality Systems: Dedicated to GMP Manufactureby AgilentLife228 views
- 6:49
Duchenne Muscular Dystrophyby kellyandsherri10,351 views
- 5:15
Living With Duchenne Muscular Dystrophyby clicker00914,255 views
- 4:45
Muscular Dystrophy: A Cellular Ballad in Clayby TheKgilvi3925 views
- 3:10
Duchenne muscular dystrophyby iangriff200759,479 views
Dear Sir, i am from philippines 21 years old im suffering from DMD.,I want to request you sir,.please help me to find cure about my disease.,im hoping that one day i can walk-dance-jump and run again this is the bigger dream of my life..im so very exciting about the first targeted treatment success for DMD.. Sir please grant my request..God Bless..
MrRealxx 3 months ago
Sir, I am from India and my 14 years old son is suffering from DMD. I want to request you sir that please do try to find cure as early as possible, because my son and many other children having this disease are facing lot of problems, and they are gradually losing their lives at the early stage of life. We can't see their pain and trouble. We are feeling so helpless that we to go, what to do for our son...
Sir, please I request to all of you doctors, scientist that please try to feel our pain.
hhparmar2 4 months ago
Very exciting news.
MontroseAccess 6 months ago
Freakin awesome :D Im stoked!
Drummerjazz7 7 months ago