Haemophilia gene therapy breakthrough (UCL)

A gene therapy study developed by Dr Amit Nathwani (UCL Cancer Institute) and colleagues in collaboration with St. Jude Children's Research Hospital, Memphis, Tennessee, has shown that adults with haemophilia B benefit from the treatment, reducing need for injections with clotting factor to prevent bleeds. The findings of the six-person study mark the first evidence that gene therapy can reduce disabling, painful bleeding episodes in patients with the inherited blood disorder.

Further information:
Downloadable audio podcast: http://bit.ly/tpgZ4e
BBC News: http://bit.ly/sMPUHn
New York Times: http://bit.ly/twldkJ
UCL press release: http://bit.ly/v5xtmE

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[coppersulphate002]

Is this university a good place to study?

[UCLTV]

Well, if you ask our opinion, yes. If you want to find out more, look up our 'About UCL' site. It has info on what it's like to study here and how well we do in the rankings of universities worldwide. For more on a specific course you're interested in, look at UCL's Prospective Students page. Good luck!

[OlivierVid73]

Would hemophiliacs who develop inhibitor be able to benefit from this treatment?

[UCLTV]

- As only the producer of the video, I'm sorry that I can't answer your question. But if you want to read more, click on the link under the video to the UCL press release; that has a link to the original article in the New England Journal of Medicine, where this research was published. Good luck! I hope you find the answer. Rob

[Starsgoalie]

What about Haemophilia A - Factor VIII deficiency, can this treatment be applied to it in the same way?

[UCLTV]

- At the moment, no. Scientists do hope to apply this same method of gene therapy in the very near future to Haemophilia A, as well as diabetes and liver cancer.

[Captain Leung]

and i need this video as reference :)

[Captain Leung]

I'm doing my biology coursework and writing Hb gene therapy as a part of it. think i may apply for this uni next year :)

[HAEMOPHILIACShome]

waitin for it to b a success for H A too and for all d diseases which hav no treatment.



[coppersulphate002]

I wanted the opinion of students who have studied there and what their experiences were.

I think its biased that a representative from the UCL would say that its good university....but thanks!

[jesus garcia]

I have mild hemophilia A and I'm hoping for the day where someone comes close or to a cure or maybe myself :)

[xstudgames]

i have haemophlia and it fine and i have savvr

[provokehate]

my sone is dying from this factor 5 he is having his left leg amputated because where he lives there is no doctor who knows how to help him what can i do