Sickle Cell Anemia -- Hope from Gene Therapy

[rikhobra]

So i read here that 72 Patients are undergoing trail by the therepy as mentioened in the video here. can nay one tell the status of those 72 SCD patients.

When will this therapy be avaliable for commom man.

I have a sone 3 and a half year ols son who is having this problem. it is difficult to see him inthe problem.

[ezballer22]

Quick question for those who know their genetics. Will Chris's kids have sickle cell even though he has been treated for it?

[STFUNOOBZZ]

@ezballer22 There is a possibility. He may carry 'the sickle-cell anemia trait', which means that he carries the gene for this genetic defect. This means will give the trait to his children (which means that his kids will also carry the risk of having children with sickle cell anemia). If he has children with another person with sickle cell anemia, his children will most likely have sickle cell anemia. Hope this helps :)

[SufferInJuly]

Cancer is a disease, a chronic metabolic disease akin to other chronic metabolic diseases such as scurvy, night blindness, pellagra & pernicious anemia. No such disease has ever been cured through mechanical manipulation of the body. Where cancer is seated isn't relevant to its cure. The preventative, cure & treatment of this vitamin-deficiency disease is Amygdalin (vitamin B17). People who get at least 100 m.g. of B17 daily cannot contract cancer. It works for sickle cell anemia too.

[eagleeye2391]

my ex gf has sickle cell

[Shaela69]

I am 2 out of 4 kids. My older sister and the youngest of my little brothers have sickle cell anemia. I have sickle cell trait and my other brother doesnt have either.

[xBattleHeartx]

Sickle cell anemia VIRUS! FTW! Come on Government scientists!!

[Freshhhhh1982]

RNA interference via siRNAs may be a viable option for treatment.

[thecrazywierdo14]

i have a friend with sickle cell anemia

[BioGuelph]

The hardest thing in gene therapy was never selecting the right gene, but finding or making the right virus to act as your vector. If you get it wrong the treatment could easily kill the patient or they may start developing cancerous cells. Luckily vector testing techniques are improving every day, and targeting only specified tissues.

[drjj10]

reaserch may be proceding right as we type, but i am sure that it won't b available for a while. once they test it on mice doesn't mean it will work right away on humans. but there is hope!!

[2468Shock]

Humans have 2 Cells suppose to be 2 Normal Cells. Anemia people have 1 cell Alpha Anemia, 1 Cell Beta lower Anemia Cell or Thalasemia which is a Lower Anemia. A Person with Anemia & a Normal cell will live past 80 years a Anemia & Thalasemia will live to 15 to 28.

[webothgowrongx33]

4:00 That is the cutest baby EVER!

[MrsEntertainmentOnly]

My son has sickle cell disease, to know that it is a possible cure is a blessing...I've watched my brother suffer and have all his major organs shut down just a few days before his death in 2008...he was 2 days passed his 29th birthday...rest in peace Jonathan Parker I will always love you and miss you!

[drerror]

@MrsEntertainmentOnly May your brother RIP :)

[ominecence37]

I wish they offered this to my mother instead of letting her die in all that pain when their was a possible cure.

[insaintraining]

I'm sorry you had to endure that alongside her.

[DarkRain9000]

wow gene therapy seems to be the answer to everything. I hear gene therapy can be used to cure HIV too.

[yippeee4]

research ongoing with 72 patients worldwide

[samsungbx]

i frome france i have sickle cell , it's possible translate in french please

[vculifesciences]

Unfortunately, we are not providing translation services for the videos at this point. Sorry for any inconvenience.

[michaelgniewek]

This is a very one-sided review video. Although the treatment may be break through and incredible for future treatment, using a Virus as a vector is scary...a mutation could occur and who knows what could happen.

[DarkRain9000]

i'm thinking scientists use very weak viruses like those use in vaccines to minimize the worst case scenario.

[yippeee4]

the viruses have all their dangerous components extracted. They're basically just empty vesicles containing only the human genome and the bare neccesities in the viral genome to keep it alive until it donates the genome to the target cell.

[Lightswicth]

I HAVE SCA AND I WOULD NEVER GET IT Theres like a chance you can die and you have to take meds every day and find a donor too much work not worth it to me

[xcaramel24]

i have a friend who got this and now they have leukemia so researh b4 thinking about gettn it